Families are elated by news of the first treatment for Huntington's disease - but when and how will the NHS fund it?

However, in late September 2025, scientists successfully treated Huntington’s for the first time in a ground-breaking study.

Pivotal results from uniQure’s gene therapy for Huntington’s disease have brought new light to patients who have known only ...

The FDA is said to be making a U-turn on uniQure’s one-time gene therapy candidate for Huntington’s disease despite the treatment being hailed as a game-changer. | FDA is said to be making a U-turn on ...

Huntington’s disease (HD) is one of those rare conditions that affects not just the patient but the entire family—medically, emotionally and genetically. This inherited brain disorder causes gradual ...

Researchers in the United Kingdom say they have successfully trialed what could become the world's first gene therapy for Huntington's disease – a fatal neurodegenerative disorder that is typically ...

TAMPA, Fla. (WFLA) — For the first time, scientists have successfully treated someone suffering from Huntington’s disease, a fatal genetic illness with no cure. The Mayo Clinic reports that the ...

Huntington’s disease (HD) is a condition that is hereditary and causes nerve cells in specific parts of the brain to slowly deteriorate and die. The disorder affects regions responsible for controlled ...

Preliminary results from a small trial offer the clearest evidence yet that the brain disease’s progression can be slowed. A one-time gene therapy can markedly slow the progression of Huntington’s ...

UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...