An 11-year-old girl with muscular dystrophy was given a cheer as she walked down the hallway of Southampton Hospital as part ...

Stanford Medicine researchers found that a smartphone could monitor patients with two types of muscular dystrophy as well as ...

A long-running confirmatory trial of two of Sarepta Therapeutics’ Duchenne muscular dystrophy drugs has missed its main goal.

Sarepta said on Monday that its late-stage study testing two gene-targeted therapies for Duchenne muscular dystrophy did not ...

An 11-year-old girl with muscular dystrophy was given a cheer as she walked down the hallway of Southampton Hospital as part of an inspiring challenge.

Researchers from Leiden University Medical Center and the University of Florida have found hundreds of blood proteins in ...

Because researchers have made such striking progress in developing drugs to treat neuromuscular diseases, Scott Delp, Ph.D., ...

This novel therapy offers the first FDA-approved option to address the root cause of this ultra-rare condition, which causes progressive muscle weakness impairing walking, breathing, and swallowing.

His parents Stephen and Jenny have asked Sheffield Children's NHS Foundation Trust to approve the use of drug givinostat, ...

But if a boy with muscular dystrophy just wants to walk again, he’s in trouble. That’s the outcome of the state’s high-cost drug initiative, which empowers the state’s Department of Health to ...

BridgeBio said an experimental therapy for a rare form of muscular dystrophy succeeded in a key trial, potentially setting up ...

An Omaha woman battling a disabling disease says she had been caught in the middle of a billing dispute. Notices from a ...