One of the most devastating diseases finally has a treatment that can slow its progression and transform lives, tearful ...
Victor Sung, M.D., director of the Division of Movement Disorders in the University of Alabama at Birmingham Department of ...
UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...
TAMPA, Fla. (WFLA) — For the first time, scientists have successfully treated someone suffering from Huntington’s disease, a fatal genetic illness with no cure. The Mayo Clinic reports that the ...
As well as slowing disease progression by 75 percent at 36 months, the scientists found that neurofilament light protein (NfL)—a biomarker of neuronal damage—levels in spinal fluid were lower in ...
An experimental gene therapy slowed Huntington’s by up to 75 percent in a small clinical trial. While not a cure, it may give patients longer lives.
Relatives of those affected by Huntington's disease have said they now have hope for the future after the discovery of a treatment which could slow the disease by 75%. The hereditary illness ...
“Beyond UniQure, the pipeline includes highly promising approaches that will ideally move the goal from merely managing ...
Researchers in the United Kingdom say they have successfully trialed what could become the world's first gene therapy for Huntington's disease – a fatal neurodegenerative disorder that is typically ...