L.A. and Paris-based Vendôme Pictures, producer of Oscar Best Picture winner Coda, has unveiled the cast for previously ...
Dosing has begun in a long-term extension study testing Satellos Bioscience’s experimental oral therapy SAT-3247 in men with ...
Because researchers have made such striking progress in developing drugs to treat neuromuscular diseases, Scott Delp, Ph.D., ...
A long-running confirmatory trial of two of Sarepta Therapeutics’ Duchenne muscular dystrophy drugs has missed its main goal.
Stanford Medicine researchers found that a smartphone could monitor patients with two types of muscular dystrophy as well as ...
Sarepta said on Monday that its late-stage study testing two gene-targeted therapies for Duchenne muscular dystrophy did not ...
This novel therapy offers the first FDA-approved option to address the root cause of this ultra-rare condition, which causes progressive muscle weakness impairing walking, breathing, and swallowing.
An 11-year-old girl with muscular dystrophy was given a cheer as she walked down the hallway of Southampton Hospital as part ...
Newport Beach-based CureDuchenne, a global nonprofit dedicated to funding and finding a cure for Duchenne muscular dystrophy, ...
BridgeBio said an experimental therapy for a rare form of muscular dystrophy succeeded in a key trial, potentially setting up ...
“Kids with Duchenne muscular dystrophy, mostly boys, lose the ability to walk in their early teens,” Raffone said. “They lose ...
His parents Stephen and Jenny have asked Sheffield Children's NHS Foundation Trust to approve the use of drug givinostat, ...
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